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VIEWPOINTS_Dr. Jay Backstrom_2023

Dr. Jay Backstrom shares insights from the Phase II TOPAZ trial for the treatment of SMA

Shots:  Dr. Jay Backstrom in an engaging conversation with PharmaShots, shares the highlights of the P-II Topaz trial designed to evaluate the safety and efficacy of apitegromab for the treatment of Spinal Muscle Atrophy (Type 2 & 3)   With the potential to transform care in SMA by directly addressing progressive muscle weakness, apitegromab aims to…

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Exclusive_Nagesh Mahanthappa_2022

Nagesh Mahanthappa, Interim CEO of Scholar Rock Shares Insights on Treatment Options for Spinal Muscular Atrophy

Shots: Nagesh talked about how Spinal Muscular Atrophy (SMA) is affecting people all over the world and how Scholar Rock’s treatment options are improving the lives of those living with this disease Nagesh also spoke about Scholar Rock’s lead product in SMA, apitegromab, highlighting its trial designs (TOPAZ & SAPPHIRE trials), outcomes, and real-world data…

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