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Chiesi Group Enters a ~$2.1B Deal with Arbor Biotechnologies to Develop Novel Rare Disease Gene Editing Programs

Shots: Chiesi Group has entered into an exclusive global collaboration & license deal with Arbor for ABO-101 in primary hyperoxaluria type 1 (PH1) & a multitarget option to use Arbor’s gene editing platform for developing liver-targeted therapies for rare diseases As per the deal, Chiesi will obtain exclusive rights to develop & commercialize ABO-101 for PH1…
4 hours ago

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Disease of the Month – Gaucher Disease
INSIGHTS+

Disease of the Month – Gaucher Disease

Shots:  Gaucher disease is a rare, autosomal recessive disorder that enlarges organs like the bone marrow, liver, and spleen by depositing fats (lipids) in them  In this reprise of our Disease of the Month report, we present an enlightening description of Gaucher disease with a thorough study of epidemiology, market size, disease management, potential medicines,…
August 28, 2024

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New Drug Designations - September 2023
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New Drug Designations – September 2023

Shots:  PharmaShots' designation report provides a concise overview of several drugs and their designations by the US FDA, the EU, and China. This month’s report includes 10 biological drugs, 15 small molecules, 5 cell and gene therapies, 4 devices, 1 vaccine and 1 microbiota  MicuRx’ Contezolid and Contezolid acefosamil, focused on the treatment of Diabetic…
October 16, 2023

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VIEWPOINTS_Martin Mackay_2023
VIEWPOINTS

Martin Mackay, CEO of Rallybio, Shares his Thoughts on the Appointment of Jonathan I. Lieber as Chief Financial Officer

Shots: Martin shared his views on the appointment of Jonathan I. Lieber as the CFO of Rallybio. Martin spoke about Jonathan's educational background and experience while talking to PharmaShots' team He also talked about how Jonathan I. Lieber’s expertise in finance, capital raising, long-range strategic planning, operations, and investor relations can contribute to the long-term…
April 10, 2023

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PharmaShots Interview Insmed’s Martina Flammer Shares Insights on New Affordable Drugs for Rare Diseases
VIEWPOINTS

PharmaShots Interview: Insmed’s Martina Flammer Shares Insights on New Affordable Drugs for Rare Diseases

In an interview with PharmaShots, Martina Flammer, Chief Medical Officer at Insmed share her views on the R&D continuum to develop new drugs for rare diseases and also highlights its business pillars Shots: The idea of the continuum is that all department works together to develop the drugs which will be helpful not only for the company but for patients too In…
January 11, 2022

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