Shots:
Health Canada has approved PTC's Sephience (sepiapterin) for the treatment of phenylketonuria (PKU) in pts of all ages, with broad labeling for hyperphenylalaninemia in pts (≥1mos.) with sepiapterin-responsive PKU
Approval was based on APHENITY study results & long-term extension data showing durable effects & favorable safety in PKU pts
Sephience is a natural precursor…
