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Rocket Presents Results of RP-L201 in the P-II Trial for the Treatment of Severe Leukocyte Adhesion Deficiency-I at ASGCT 2022

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Rocket Presents Results of RP-L201 in the P-II Trial for the Treatment of Severe Leukocyte Adhesion Deficiency-I at ASGCT 2022

Rocket Presents Results of RP-L201 in the P-II Trial for the Treatment of Severe Leukocyte Adhesion Deficiency-I at ASGCT 2022

Shots:

  • The P-II trial evaluates the safety & efficacy of RP-L201 in patients with sev. LAD-I
  • At the data cut-off of Mar 2022, the results showed a sustained CD18 restoration & expression on ≥10% of neutrophils in all 9 patients aged 5mos. to 9yrs. @ 3 to 24mos. of follow-up after RP-L201 infusion, 100% OS @1yr. post-infusion via Kaplan, reduction in the rate of all-cause hospitalizations & sev. inf., resolution of LAD-I-related skin rash & restoration of wound repair capabilities along with sustained phenotypic correction
  • The safety profile was favorable in all patients with no RP-L201-related serious AEs. The company is expected to file an application in H1’23, following discussions with health authorities

Ref: Businesswire | Image: Rocket

Click here to­ read the full press release 

Neha

Neha is a Senior Editor at PharmaShots. She is passionate and very enthusiastic about recent updates and developments in the life sciences and pharma industry. She covers Biopharma, MedTech, and Digital health segments along with different reports at PharmaShots. She can be contacted at connect@pharmashots.com.

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