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Ultragenyx Entered into an Exclusive License Agreement with Abeona for ABO-102 (UX111) to Treat Sanfilippo Syndrome Type A

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Ultragenyx Entered into an Exclusive License Agreement with Abeona for ABO-102 (UX111) to Treat Sanfilippo Syndrome Type A

Shots:

  • Abeona is eligible to receive commercial milestones along with royalties of ~10% on net sales. Ultragenyx obtains global rights for ABO-102
  • The company presented the interim results from the (Transpher A) trial at ASGCT 2022 which showed the neurocognitive development in children aged 2yrs. or with DQ > 60 along with continued or stabilized cognitive function & behavioral progress, increase in cortical gray matter, total cerebral & amygdala volumes
  • Additionally, reduction in liver volume, CSF fluid & plasma heparan sulfate, was well-tolerated with no TRAEs & SAEs, ABO-102 has received RMAT, FTD, ODD & RPD designation from the US FDA while PRIME & Orphan medicinal product designations from the EMA

Ref: Ultragenyx | Image: Ultragenyx 

Click here to­ read the full press release 

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Neha is a Senior Editor at PharmaShots. She is passionate and very enthusiastic about recent updates and developments in the life sciences and pharma industry. She covers Biopharma, MedTech, and Digital health segments along with different reports at PharmaShots. She can be contacted at connect@pharmashots.com.

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