Acceleron's ACE-083 Receives FDA's ODD for Charcot Marie Tooth Disease (CMT)
Shots:
- The ODD designation follows two P-II studies assessing ACE-083 (Myostatin+ muscle agent) in patients with CMT and facioscapulohumeral muscular dystrophy (FSHD)
- The two P-II studies demonstrated in elevation in muscle volume in target muscles with its expected results in H2’19 for CMT & FSHD
- ACE-083 is a long acting Myostatin+ muscle agent targeting TGF-beta superfamily ligands and has receives FDA’s FT designation for CMT and FDA’s FT & ODD for FSHD in 2018
Ref: Ascendis Pharma | Image: Cape Business News
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