Shots:

• St. Jude Children’s Research Hospital out-licenses exclusive worldwide rights for Lentiviral Gene Therapy for X-linked Severe Combined Immunodeficiency also known as “bubble boy”
• This therapy is presently being assessed in a phase I/II multicenter study in infants (Age ≥2)
•  In Interim Analysis- 6/8 patients achieved reconstituted immune system within 3-4 mos of treatment- in addition to tolerability

Ref: Mustang Bio | Image: Twitter